Amicus Therapeutics, Inc. (NASDAQ:FOLD) Receives Positive FED For Fabry Disease Treatment

1201
Amicus Therapeutics Inc

Amicus Therapeutics, Inc. (NASDAQ:FOLD) recently announced that National Institute for Health and Care Excellence (NICE) has provided its positive insight for GALAFOLD™ (MIGALASTAT), as a treatment for Fabry Disease, in England. The company stated that NICE’s Highly Specialised Technologies Evaluation Committee (EC)’s final evaluation determination (FED) has come with valuable insights.

NICE recommended commissioning Galafold in England for the purpose of National Health Service (NHS). It is important to note here that Galafold will be used within NHS as a first-line therapy treatment for adolescents aged 16 years and above, along with adults, for a longer duration.

This will be used as a treatment among patients where Fabry disease has been confirmed on diagnosis. This is an alpha-galactosidase A deficiency disease among people with amenable mutation. In the early months of this year, the company plans to bring the treatment in Northern Ireland, Wales and England.

First oral medicine for Fabry disease in the UK

The CEO and Chairman of company, John F. Crowley said that NICE’s positive FED is a significant step towards the patients suffering from Fabry in the UK. On being introduced in the markets there, Galafold will become the first oral medicine in the UK, for patients aged 16 years and above.

The evaluation process included Fabry patients themselves, advocacy groups and physician experts. The CEO stated that the company was moving faster now, in making available, Galafold, as a commercial medicine in the U.K.

The European Commission’s Approval

Earlier in May 2016, the medicine was given a full approval in the form of first line therapy for Fabry patients. The European Commission had agreed unanimously to approve the medicine for long-term treatment, among the aforesaid having amenable mutation.

The company’s collaboration with Fabry community is getting it commercial markets with 100% approvals. This new oral treatment will play a vital role in treating these patients.

This made 2017, an important year for company since the good news came right in the first week.

Subscribe to get your free report!

* indicates required
*Past performance is not a predictor of future results. All investing involves risk of loss and individual investments may vary. The examples provided may not be representative of typical results. Your capital is at risk when you invest – you can lose some or all of your money. Never risk more than you can afford to lose.By submitting your information you agree to the terms of our Privacy Policy • Cancel Newsletter Any Time.This is a FREE service from Finacials Trend. Signing up for our FREE daily e-letter also entitles you to receive this report. We will NOT share your email address with anyone.